1[期刊论文]

Full-Length Dystrophin Reconstitution with Adeno-Associated Viral Vectors

作者：William Lostal ;Kasun Kodippili ;Yongping Yue 等

来源：Human Gene Therapy. 2014 ;25(6):552-562.doi:10.1089/hum.2013.210

出版社：Mary Ann Liebert Inc

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2[期刊论文]

Minimal Consequences of CMAH and DBA/2J Background on a FKRP Deficient Model

作者：Camille Vaubourg ;Evelyne Gicquel ;Isabelle Richard 等

来源：Journal of Neuromuscular Diseases. 2021 ;8(5):1-9.doi:10.3233/JND-200487

出版社：IOS Press

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3[期刊论文]

Long-Term Robust Myocardial Transduction of the Dog Heart from a Peripheral Vein by Adeno-Associated Virus Serotype-8

作者：Xiufang Pan ;Yongping Yue ;Keqing Zhang 等

来源：Human Gene Therapy. 2013 ;24(6):584-594.doi:10.1089/hum.2013.044

出版社：Mary Ann Liebert Inc

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4[期刊论文]

Assessment of Therapeutic Potential of a Dual AAV Approach for Duchenne Muscular Dystrophy

作者：Sonia Albini ;Laura Palmieri ;Auriane Dubois 等

来源：International Journal of Molecular Sciences. 2023 ;24(14):11421.doi:10.3390/ijms241411421

出版社：MDPI AG

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5[期刊论文]

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

作者：David Israeli ;Jérôme Poupiot ;Fatima Amor 等

来源：Scientific Reports. 2016 ;6.doi:10.1038/srep28097

出版社：Springer Nature

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6[期刊论文]

Circulating miRNAs are generic and versatile therapeutic monitoring biomarkers in muscular dystrophies

作者：David Israeli ;Jérôme Poupiot ;Fatima Amor 等

来源：Scientific Reports. 2016 ;6(1).doi:10.1038/srep28097

出版社：Springer Nature

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7[期刊论文]

Efficient recovery of dysferlin deficiency by dual adeno-associated vector-mediated gene transfer

作者：William Lostal ;Marc Bartoli ;Nathalie Bourg 等

来源：Human Molecular Genetics. 2010 ;19(10):1897-1907.doi:10.1093/hmg/ddq065

出版社：Oxford University Press (OUP)

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8[期刊论文]

Single SERCA2a Therapy Ameliorated Dilated Cardiomyopathy for 18 Months in a Mouse Model of Duchenne Muscular Dystrophy

作者：Nalinda B. Wasala ;Yongping Yue ;William Lostal 等

来源：Molecular Therapy. 2020 ;28(3):845-854.doi:10.1016/j.ymthe.2019.12.011

出版社：Elsevier BV

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9[期刊论文]

Titin M-line insertion sequence 7 is required for proper cardiac function in mice

作者：Ariane Biquand ;Simone Spinozzi ;Paola Tonino 等

来源：Journal of Cell Science. 2021 ;134(18).doi:10.1242/jcs.258684

出版社：The Company of Biologists

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10[期刊论文]

Co-Administration of Simvastatin Does Not Potentiate the Benefit of Gene Therapy in the mdx Mouse Model for Duchenne Muscular Dystrophy

作者：Nathalie Bourg ;Ai Vu Hong ;William Lostal 等

来源：International Journal of Molecular Sciences. 2022 ;23(4):2016.doi:10.3390/ijms23042016

出版社：MDPI AG

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